Statements (17)
Predicate | Object |
---|---|
gptkbp:instanceOf |
gene therapy
|
gptkbp:administeredBy |
intravenous infusion
|
gptkbp:alternativeName |
gptkb:fidanacogene_elaparvovec
|
gptkbp:clinicalTrialPhase |
Phase 3
|
gptkbp:developedBy |
gptkb:Spark_Therapeutics
|
gptkbp:geneDelivered |
gptkb:Factor_IX_(F9)
|
https://www.w3.org/2000/01/rdf-schema#label |
SPK-9001
|
gptkbp:indication |
treatment of hemophilia B
|
gptkbp:intendedUse |
increase Factor IX activity
|
gptkbp:mechanismOfAction |
AAV vector delivering functional F9 gene
|
gptkbp:routeOfAdministration |
intravenous
|
gptkbp:sponsor |
gptkb:Pfizer
|
gptkbp:status |
investigational
|
gptkbp:target |
gptkb:hemophilia_B
|
gptkbp:vectorFor |
gptkb:AAV_(adeno-associated_virus)
|
gptkbp:bfsParent |
gptkb:Spark_Therapeutics
|
gptkbp:bfsLayer |
7
|