Statements (18)
| Predicate | Object |
|---|---|
| gptkbp:instanceOf |
gene therapy
investigational drug |
| gptkbp:alternativeName |
gptkb:SPK-9001
PF-06838435 |
| gptkbp:clinicalTrialPhase |
Phase 3
|
| gptkbp:deliveryVector |
adeno-associated virus (AAV)
|
| gptkbp:developedBy |
gptkb:Pfizer
gptkb:Spark_Therapeutics |
| gptkbp:hasINN |
gptkb:fidanacogene_elaparvovec
|
| https://www.w3.org/2000/01/rdf-schema#label |
fidanacogene elaparvovec
|
| gptkbp:indication |
gptkb:hemophilia_B
|
| gptkbp:mechanismOfAction |
delivers functional copy of F9 gene
|
| gptkbp:routeOfAdministration |
intravenous
|
| gptkbp:status |
investigational
|
| gptkbp:targetGene |
gptkb:F9
|
| gptkbp:therapeuticArea |
hematology
|
| gptkbp:bfsParent |
gptkb:SPK-9001
|
| gptkbp:bfsLayer |
8
|