uniQure Biopharma N.V.

GPTKB entity

Properties (54)
Predicate Object
gptkbp:instanceOf gptkb:Company
gptkbp:acquisition AAV-based gene therapy platform
Chimerix's_gene_therapy_assets
Glybera_rights_from_the_European_Commission
gptkbp:CEO gptkb:Matthijs_P._H._H._van_der_Meer
gptkbp:clinicalTrials gptkb:Hemophilia_B
gptkb:Fabry_disease
gptkb:Huntington's_disease
Phase 2
Phase 3
Phase 1/2
Gene therapy for Pompe disease
Gene therapy for beta-thalassemia
Gene therapy for cystic fibrosis
Gene therapy for hemophilia B
Gene therapy for sickle cell disease
Gene therapy for spinal muscular atrophy
Liver-directed gene therapy
Adeno-associated_virus_gene_therapy
Gene_therapy_for_Duchenne_muscular_dystrophy
Gene_therapy_for_Fabry_disease
Gene_therapy_for_Huntington's_disease
gptkbp:collaborations gptkb:Duke_University
gptkb:Harvard_University
gptkb:University_of_Pennsylvania
gptkbp:employeeCount 200+
gptkbp:focus gene therapy
gptkbp:founded 1991
gptkbp:headquarters Amsterdam,_Netherlands
https://www.w3.org/2000/01/rdf-schema#label uniQure Biopharma N.V.
gptkbp:investmentFocus $50 million Series B funding
$100 million funding round
$75 million Series C funding
gptkbp:market $1.5 billion
gptkbp:partnerships gptkb:AstraZeneca
gptkb:Boehringer_Ingelheim
gptkb:Bristol-Myers_Squibb
Novartis
Regenxbio
gptkbp:products gptkb:Glybera
AMT-061
AMT-130
gptkbp:regulatoryCompliance European_Medicines_Agency_(EMA)_for_Glybera
FDA_for_AMT-061
gptkbp:research_areas genetic disorders
rare diseases
metabolic diseases
gptkbp:researchFocus gptkb:Adeno-associated_virus_(AAV)_vectors
gptkbp:researchInterest gptkb:Lexington,_Massachusetts
Amsterdam,_Netherlands
gptkbp:stockSymbol QURE
gptkbp:subsidiary gptkb:uniQure_N.V.
gptkbp:tradedOn gptkb:NASDAQ
gptkbp:website www.uniqure.com