Statements (18)
Predicate | Object |
---|---|
gptkbp:instanceOf |
gptkb:chemical_compound
gptkb:drug |
gptkbp:ATCCode |
none
|
gptkbp:CASNumber |
2098603-46-2
|
gptkbp:developedBy |
gptkb:Dicerna_Pharmaceuticals
|
gptkbp:drugClass |
gptkb:small_interfering_RNA_(siRNA)
|
gptkbp:hasMolecularFormula |
C27H32N8O13P2S2
|
gptkbp:hasUNII |
1Q1K1N2J1F
|
https://www.w3.org/2000/01/rdf-schema#label |
Nedosiran
|
gptkbp:indication |
gptkb:primary_hyperoxaluria
|
gptkbp:mechanismOfAction |
gptkb:RNA_interference
|
gptkbp:PubChem_CID |
137517073
|
gptkbp:routeOfAdministration |
subcutaneous injection
|
gptkbp:status |
investigational drug
|
gptkbp:synonym |
gptkb:DCR-PHXC
|
gptkbp:target |
gptkb:LDHA_gene
|
gptkbp:bfsParent |
gptkb:Dicerna_Pharmaceuticals
|
gptkbp:bfsLayer |
7
|