| gptkbp:instanceOf | gptkb:biotechnology 
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                                | gptkbp:acquiredBy | gptkb:Global_Gene_Therapy_Manufacturing_Facility gptkb:Myonexus_Therapeutics
 Lacerta Therapeutics (partial stake)
 
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                                | gptkbp:CEO | gptkb:Douglas_S._Ingram 
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                                | gptkbp:collaboratesWith | gptkb:Duke_University gptkb:Roche
 gptkb:Nationwide_Children's_Hospital
 
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                                | gptkbp:country | gptkb:United_States 
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                                | gptkbp:focusesOn | rare diseases genetic medicine
 RNA-targeted therapeutics
 
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                                | gptkbp:founded | 1980 
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                                | gptkbp:founder | gptkb:James_E._Summerton 
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                                | gptkbp:headquartersLocation | gptkb:Cambridge,_Massachusetts,_United_States 
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                                | gptkbp:industry | gptkb:biotechnology 
 | 
                        
                            
                                | gptkbp:listedOn | gptkb:NASDAQ_Biotechnology_Index gptkb:S&P_400
 
 | 
                        
                            
                                | gptkbp:marketCap | multi-billion USD 
 | 
                        
                            
                                | gptkbp:milestone | first FDA-approved therapy for Duchenne muscular dystrophy 
 | 
                        
                            
                                | gptkbp:notableProduct | gptkb:Amondys_45 gptkb:Elevidys
 gptkb:Exondys_51
 gptkb:Vyondys_53
 
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                                | gptkbp:numberOfEmployees | 2023 over 900
 
 | 
                        
                            
                                | gptkbp:parentCompany | independent 
 | 
                        
                            
                                | gptkbp:patent | gene editing RNA-based therapeutics
 
 | 
                        
                            
                                | gptkbp:previousName | gptkb:AVI_BioPharma gptkb:AntiVirals_Inc.
 
 | 
                        
                            
                                | gptkbp:publiclyTraded | true 
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                                | gptkbp:regulates | gptkb:FDA 
 | 
                        
                            
                                | gptkbp:researchArea | RNA splicing antisense oligonucleotides
 
 | 
                        
                            
                                | gptkbp:specializesIn | gptkb:gene_therapy gptkb:Duchenne_muscular_dystrophy
 precision genetic medicine
 
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                                | gptkbp:stockExchange | gptkb:NASDAQ 
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                                | gptkbp:stockSymbol | gptkb:NASDAQ gptkb:SRPT
 
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                                | gptkbp:therapeuticArea | neuromuscular diseases rare pediatric diseases
 
 | 
                        
                            
                                | gptkbp:website | https://www.sarepta.com/ 
 | 
                        
                            
                                | gptkbp:bfsParent | gptkb:Dyno_Therapeutics 
 | 
                        
                            
                                | gptkbp:bfsLayer | 6 
 | 
                        
                            
                                | https://www.w3.org/2000/01/rdf-schema#label | Sarepta Therapeutics 
 |