Statements (22)
| Predicate | Object |
|---|---|
| gptkbp:instanceOf |
gptkb:drug
|
| gptkbp:approvalYear |
2019
|
| gptkbp:approvedBy |
gptkb:FDA
|
| gptkbp:ATCCode |
M09AX10
|
| gptkbp:CASNumber |
1446729-34-7
|
| gptkbp:developedBy |
gptkb:Sarepta_Therapeutics
|
| gptkbp:exonTargeted |
exon 53
|
| gptkbp:form |
solution for injection
|
| gptkbp:genericName |
golodirsen
|
| gptkbp:hasMolecularFormula |
C615H941N173O176P30
|
| https://www.w3.org/2000/01/rdf-schema#label |
Vyondys 53
|
| gptkbp:indication |
gptkb:Duchenne_muscular_dystrophy
|
| gptkbp:legalStatus |
prescription only
|
| gptkbp:mechanismOfAction |
exon skipping
|
| gptkbp:orphanDrugStatus |
yes
|
| gptkbp:pregnancyCategory |
not assigned
|
| gptkbp:routeOfAdministration |
intravenous
|
| gptkbp:synonym |
SRP-4053
|
| gptkbp:targetGene |
gptkb:DMD_gene
|
| gptkbp:UNII |
6H4G63K35Q
|
| gptkbp:bfsParent |
gptkb:Sarepta_Therapeutics
|
| gptkbp:bfsLayer |
7
|