Statements (28)
| Predicate | Object |
|---|---|
| gptkbp:instanceOf |
gptkb:drug
|
| gptkbp:approvalYear |
2016
|
| gptkbp:approvedBy |
gptkb:FDA
|
| gptkbp:ATCCode |
gptkb:M09AX07
|
| gptkbp:CASNumber |
1173755-55-4
|
| gptkbp:countryOfOperation |
gptkb:United_States
|
| gptkbp:form |
solution for injection
|
| gptkbp:genericName |
eteplirsen
|
| gptkbp:hasMolecularFormula |
C365H570N176O139P30
|
| https://www.w3.org/2000/01/rdf-schema#label |
Exondys 51
|
| gptkbp:indication |
gptkb:Duchenne_muscular_dystrophy
|
| gptkbp:legalStatus |
prescription only
|
| gptkbp:manufacturer |
gptkb:Sarepta_Therapeutics
|
| gptkbp:mechanismOfAction |
exon skipping
|
| gptkbp:orphanDrugStatus |
yes
|
| gptkbp:pregnancyCategory |
not assigned
|
| gptkbp:prescriptionStatus |
Rx only
|
| gptkbp:routeOfAdministration |
intravenous
|
| gptkbp:sideEffect |
fever
vomiting headache cough arthralgia balance disorder |
| gptkbp:target |
exon 51 of the DMD gene
|
| gptkbp:UNII |
6H4E3KUA2T
|
| gptkbp:bfsParent |
gptkb:Sarepta_Therapeutics
|
| gptkbp:bfsLayer |
7
|