gene therapy for hemophilia

GPTKB entity

Properties (59)
Predicate Object
gptkbp:instanceOf gene therapy
gptkbp:aimsTo provide long-term treatment
gptkbp:associated_with patient outcomes
high treatment costs
risks and side effects
gptkbp:basedOn genetic modification
gptkbp:clinicalTrials various stages
gptkbp:collaborations research institutions and companies
gptkbp:delivers corrected gene
gptkbp:developedBy biotechnology companies
gptkbp:explores other genetic disorders
gptkbp:features innovation in healthcare
gptkbp:future_plans improve quality of life
gptkbp:has_a_focus_on medical research
pharmaceutical research
biomedical engineering research
gptkbp:has_implications_for healthcare_policy
https://www.w3.org/2000/01/rdf-schema#label gene therapy for hemophilia
gptkbp:influenced patient genetics
gptkbp:involves ex vivo and in vivo techniques
injection into the bloodstream
gptkbp:is_a molecular medicine
gptkbp:is_a_document_that hemophilia patients
gptkbp:is_a_subject_of clinical guidelines
scientific conferences
ethical discussions
gptkbp:is_a_symbol_of different_hemophilia_types
gptkbp:is_a_time_for treatment-resistant patients
gptkbp:is_a_way_to genetic diseases
traditional therapies
gptkbp:is_displayed_on promising results
increase factor levels
gptkbp:is_essential_for hemophilia_treatment
gptkbp:is_evaluated_by long-term safety
gptkbp:is_expected_to reduce healthcare burden
transform_hemophilia_management
gptkbp:is_funded_by government grants
gptkbp:is_governed_by health authorities
gptkbp:is_linked_to advancements in biotechnology
gptkbp:is_monitored_by regulatory agencies
gptkbp:is_part_of personalized treatment plans
precision medicine
the evolving landscape of medicine
the future of genetic medicine
the_future_of_hemophilia_care
gptkbp:is_studied_in animal models
multiple countries
gptkbp:is_supported_by patient advocacy groups
gptkbp:mayHave need for regular factor replacement
gptkbp:produces gptkb:severe_hemophilia
other gene therapies.
gptkbp:reduces bleeding episodes
gptkbp:requires patient eligibility assessment
gptkbp:serves hemophilia
gptkbp:suitableFor a potential cure
gptkbp:targets liver cells
gptkbp:ticketingSystem intravenous infusion
gptkbp:uses viral vectors
gptkbp:was_a_response_to limitations of current therapies