Statements (19)
Predicate | Object |
---|---|
gptkbp:instanceOf |
gene editing therapy
|
gptkbp:clinicalTrialPhase |
gptkb:New_Zealand
gptkb:United_Kingdom gptkb:United_States Phase 1 |
gptkbp:companyStockSymbol |
gptkb:NTLA
|
gptkbp:deliveredBy |
lipid nanoparticle
|
gptkbp:developedBy |
gptkb:Intellia_Therapeutics
|
gptkbp:firstInHuman |
2021
|
gptkbp:headquartersLocation |
gptkb:Cambridge,_Massachusetts,_USA
|
https://www.w3.org/2000/01/rdf-schema#label |
NTLA-5001
|
gptkbp:mechanismOfAction |
CRISPR-Cas9 gene editing
|
gptkbp:routeOfAdministration |
intravenous
|
gptkbp:status |
investigational
|
gptkbp:target |
gptkb:transthyretin_amyloidosis
|
gptkbp:targetGene |
gptkb:TTR_gene
|
gptkbp:therapeuticArea |
rare diseases
|
gptkbp:bfsParent |
gptkb:Intellia_Therapeutics
|
gptkbp:bfsLayer |
5
|