Statements (24)
Predicate | Object |
---|---|
gptkbp:instanceOf |
gptkb:person
|
gptkbp:awardReceived |
gptkb:Rare_Champion_of_Hope_Award
gptkb:Roscoe_O._Brady_Award_for_Innovation |
gptkbp:developedBy |
Aldurazyme (laronidase)
enzyme replacement therapy for MPS I |
gptkbp:education |
gptkb:Pomona_College
gptkb:University_of_California,_Los_Angeles |
gptkbp:employer |
gptkb:Ultragenyx_Pharmaceutical
|
gptkbp:field |
genetics
pediatrics |
gptkbp:founded |
gptkb:EveryLife_Foundation_for_Rare_Diseases
|
https://www.w3.org/2000/01/rdf-schema#label |
Emil D. Kakkis
|
gptkbp:knownFor |
enzyme replacement therapy
rare disease drug development |
gptkbp:nationality |
gptkb:American
|
gptkbp:notableWork |
gptkb:Aldurazyme
founding EveryLife Foundation for Rare Diseases |
gptkbp:occupation |
gptkb:physician
gptkb:researchers biologist |
gptkbp:position |
CEO
|
gptkbp:bfsParent |
gptkb:Ultragenyx_Pharmaceutical
gptkb:Ultragenyx |
gptkbp:bfsLayer |
7
|