Statements (60)
| Predicate | Object |
|---|---|
| gptkbp:instance_of |
gptkb:Person
|
| gptkbp:affiliation |
gptkb:Nationwide_Children's_Hospital
|
| gptkbp:awards |
NINDS R01 grant
|
| gptkbp:clinical_trial |
SMA gene therapy trials
|
| gptkbp:collaborations |
gptkb:Dr._Jerry_Mendell
biotechnology companies |
| gptkbp:community_engagement |
patient advocacy groups
|
| gptkbp:contribution |
advancements in SMA treatment
|
| gptkbp:education |
gptkb:University_of_Michigan
|
| gptkbp:field |
gptkb:physicist
neurology pediatrics |
| gptkbp:goal |
improve patient outcomes
|
| gptkbp:grants |
NIH funding
|
| gptkbp:has_experience_in |
molecular biology
clinical trials therapeutic development |
| https://www.w3.org/2000/01/rdf-schema#label |
Dr. Brian Kaspar
|
| gptkbp:impact |
pediatric neurology
|
| gptkbp:influence |
SMA treatment protocols
gene therapy field |
| gptkbp:innovation |
AAV vector technology
|
| gptkbp:invention |
gene delivery systems
|
| gptkbp:is_involved_in |
clinical research
|
| gptkbp:known_for |
gene therapy research
|
| gptkbp:leadership |
scientific advisory boards
|
| gptkbp:mentor |
young researchers
|
| gptkbp:notable_performers |
gptkb:American_Society_of_Gene_and_Cell_Therapy
|
| gptkbp:notable_work |
AAV gene therapy
|
| gptkbp:position |
Chief Scientific Officer
|
| gptkbp:publishes |
gptkb:Molecular_Therapy
gptkb:Journal_of_Clinical_Investigation gptkb:Nature_Medicine |
| gptkbp:recognizes |
leading researcher in gene therapy
|
| gptkbp:research |
viral vector engineering
|
| gptkbp:research_areas |
cell biology
therapeutic interventions biomedical engineering genetic engineering therapeutic strategies molecular genetics therapeutic efficacy gene editing healthcare innovation patient-centered research disease modeling translational medicine biological therapies neurogenetics clinical genetics pediatric research therapeutic delivery systems clinical applications of gene therapy long-term outcomes in gene therapy safety assessments in gene therapy therapeutic genomics |
| gptkbp:research_focus |
neuromuscular diseases
|
| gptkbp:vision |
transformative therapies for genetic disorders
|
| gptkbp:bfsParent |
gptkb:Ave_Xis
|
| gptkbp:bfsLayer |
5
|