Statements (111)
| Predicate | Object |
|---|---|
| gptkbp:instance_of |
gptkb:Company
|
| gptkbp:acquired |
gptkb:Novartis
|
| gptkbp:advocates_for |
support initiatives
for SMA awareness. |
| gptkbp:awards |
various industry awards
various industry recognitions |
| gptkbp:ceo |
David Lennon
|
| gptkbp:clinical_trial |
ongoing
Phase 1 Phase 2 Phase 3 Phase 1, Phase 2, Phase 3 multiple sites published results innovative approaches. published in peer-reviewed journals. multiple sites in the US ongoing for multiple therapies shared with the medical community. |
| gptkbp:collaborates_with |
various academic institutions
|
| gptkbp:collaborations |
academic institutions
with universities with universities. with leading research institutions. |
| gptkbp:committee |
renowned scientists
comprised of experts in gene therapy. |
| gptkbp:community_engagement |
patient advocacy groups
|
| gptkbp:community_involvement |
awareness programs
to educate about SMA. |
| gptkbp:conference |
participates in industry events.
|
| gptkbp:employees |
over 200
|
| gptkbp:feedback |
integrated into development.
|
| gptkbp:financial_performance |
growing revenue
|
| gptkbp:focus |
gptkb:physicist
|
| gptkbp:founded |
gptkb:2013
|
| gptkbp:founder |
gptkb:Sean_Nolan
|
| gptkbp:future_plans |
expand product pipeline
expand gene therapy portfolio. focused on additional therapies. |
| gptkbp:global_presence |
international operations
operates internationally. |
| gptkbp:grants |
awarded for SMA research.
|
| gptkbp:headquarters |
gptkb:Chicago,_Illinois
|
| https://www.w3.org/2000/01/rdf-schema#label |
Ave Xis
|
| gptkbp:industry |
for gene therapy products.
part of the growing sector. |
| gptkbp:invention |
patents for gene therapy technologies.
patents on gene therapies |
| gptkbp:investment |
gptkb:Company
various venture capital firms publicly traded gene therapy market |
| gptkbp:is_effective_against |
demonstrated in clinical trials
|
| gptkbp:language_of_instruction |
multiple gene therapy candidates
multiple gene therapies |
| gptkbp:leadership |
experienced executives
|
| gptkbp:location |
gptkb:United_States
|
| gptkbp:market |
of Zolgensma.
|
| gptkbp:marketing_strategy |
expansion in global markets
|
| gptkbp:mission |
transforming the lives of patients
transform the lives of patients through gene therapy. |
| gptkbp:notable_products |
gptkb:Zolgensma
|
| gptkbp:parent_company |
gptkb:Novartis_AG
|
| gptkbp:part_of |
gptkb:Novartis_Gene_Therapies
|
| gptkbp:partnership |
with the SMA Foundation
|
| gptkbp:partnerships |
various pharmaceutical companies
biopharmaceutical companies for patient care. with providers. |
| gptkbp:platform |
AAV-based gene therapy
|
| gptkbp:population |
children with SMA
|
| gptkbp:produced_by |
state-of-the-art facilities
|
| gptkbp:production_location |
in North Carolina
|
| gptkbp:products |
strict standards
submitted for new therapies. |
| gptkbp:publishes |
gptkb:academic_journal
contributed to the field of gene therapy. |
| gptkbp:receives_funding_from |
gptkb:Company
|
| gptkbp:regulatory_compliance |
gptkb:FDA
gptkb:EMA for Zolgensma in multiple countries for new therapies. multiple submissions |
| gptkbp:research |
gptkb:Dr._Brian_Kaspar
cutting-edge research positive results |
| gptkbp:research_and_development |
gene therapies
gene therapies for neurological diseases |
| gptkbp:research_areas |
rare diseases
neuromuscular diseases gene replacement therapy |
| gptkbp:research_focus |
neuromuscular diseases
rare genetic disorders |
| gptkbp:safety_features |
extensive studies
favorable in clinical trials |
| gptkbp:scholarships |
resources for families
available for families. |
| gptkbp:social_responsibility |
community initiatives
initiatives in healthcare. |
| gptkbp:strategic_importance |
innovation in gene therapy
|
| gptkbp:student_enrollment |
clinical trials
for clinical trials. |
| gptkbp:supply_chain |
global suppliers
for gene therapy products. |
| gptkbp:technology |
AAV vector technology
|
| gptkbp:treatment |
improved patient outcomes
monitored post-approval. |
| gptkbp:website |
www.avexis.com
|
| gptkbp:bfsParent |
gptkb:onasemnogene_abeparvovec
gptkb:Zolgensma |
| gptkbp:bfsLayer |
4
|