multiple acyl-CoA dehydrogenase deficiency

GPTKB entity

Statements (32)
Predicate Object
gptkbp:instanceOf gptkb:metabolic_disorder
gptkb:inborn_error_of_metabolism
gptkbp:affects amino acid metabolism
fatty acid oxidation
choline metabolism
gptkbp:alsoKnownAs gptkb:MADD
glutaric acidemia type II
gptkbp:canBeLateOnset true
gptkbp:canBeNeonatalOnset true
gptkbp:diagnosedBy genetic testing
urine organic acid analysis
acylcarnitine profile
gptkbp:firstDescribed 1976
gptkbp:hasOrphanetID ORPHA:42
gptkbp:inheritance autosomal recessive
gptkbp:mutationAssociatedWith ETFA gene
ETFB gene
ETFDH gene
gptkbp:OMIM 231680
gptkbp:prevalence rare
gptkbp:symptom gptkb:hypoglycemia
vomiting
muscle weakness
lethargy
metabolic acidosis
hepatomegaly
gptkbp:treatment dietary management
riboflavin
carnitine supplementation
gptkbp:bfsParent gptkb:SLC25A32
gptkbp:bfsLayer 8
https://www.w3.org/2000/01/rdf-schema#label multiple acyl-CoA dehydrogenase deficiency