Statements (18)
| Predicate | Object |
|---|---|
| gptkbp:instanceOf |
gptkb:drug
|
| gptkbp:approvedBy |
gptkb:European_Union
|
| gptkbp:ATCCode |
A16AX06
|
| gptkbp:brand |
gptkb:Zavesca
|
| gptkbp:chemicalFormula |
C10H21NO4
|
| gptkbp:compatibleWith |
United States for Type C
|
| gptkbp:developedBy |
gptkb:Actelion
|
| gptkbp:legalStatus |
prescription only
|
| gptkbp:mechanismOfAction |
inhibits glucosylceramide synthase
|
| gptkbp:pregnancyCategory |
C (US)
|
| gptkbp:routeOfAdministration |
oral
|
| gptkbp:sideEffect |
diarrhea
tremor weight loss |
| gptkbp:usedFor |
gptkb:Niemann-Pick_disease_type_C
|
| gptkbp:bfsParent |
gptkb:Niemann–Pick_disease
|
| gptkbp:bfsLayer |
6
|
| https://www.w3.org/2000/01/rdf-schema#label |
miglustat (for Type C)
|