arimoclomol

GPTKB entity

Statements (32)
Predicate Object
gptkbp:instanceOf gptkb:chemical_compound
gptkb:drug
gptkbp:administeredBy oral
gptkbp:ATCCode none
gptkbp:CASNumber 289893-25-0
gptkbp:chemicalClass benzylamine derivative
hydroxyalkylamine
gptkbp:developedBy treatment of neurodegenerative diseases
gptkbp:developer Orphazyme A/S
gptkbp:EMAStatus not approved
gptkbp:hasMolecularFormula C17H25ClN2O
gptkbp:hasSMILES CC(CO)N(C)Cc1ccc(cc1OC)OC.Cl
gptkbp:hasUNII 6Z5B6HVF6O
https://www.w3.org/2000/01/rdf-schema#label arimoclomol
gptkbp:investigatedBy gptkb:Niemann-Pick_disease_type_C
amyotrophic lateral sclerosis
scleroderma
inclusion body myositis
gptkbp:IUPACName N-(2-hydroxypropyl)-3,4-dimethoxy-N-methylbenzylamine hydrochloride
gptkbp:mechanismOfAction amplifies heat shock protein expression
gptkbp:molecularWeight 324.85 g/mol
gptkbp:PubChem_CID DB12411
CHEMBL2103882
9941572
gptkbp:regulates not approved
gptkbp:routeOfAdministration oral
gptkbp:status investigational
gptkbp:synonym BRX-220
BRX-345
N-(2-hydroxypropyl)-3,4-dimethoxy-N-methylbenzylamine
gptkbp:bfsParent gptkb:Orphazyme
gptkbp:bfsLayer 8