Statements (11)
Predicate | Object |
---|---|
gptkbp:instanceOf |
gptkb:drug
|
gptkbp:developedBy |
gptkb:Stoke_Therapeutics
|
https://www.w3.org/2000/01/rdf-schema#label |
STX-801
|
gptkbp:intendedUse |
treatment of Dravet syndrome
|
gptkbp:mechanismOfAction |
upregulation of SCN1A gene expression
|
gptkbp:mode |
antisense oligonucleotide
|
gptkbp:routeOfAdministration |
intrathecal
|
gptkbp:status |
preclinical development
|
gptkbp:targetGene |
gptkb:SCN1A
|
gptkbp:bfsParent |
gptkb:Scorpion_Therapeutics
|
gptkbp:bfsLayer |
7
|