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STK-001
URI:
https://gptkb.org/entity/STK-001
GPTKB entity
Statements (14)
Predicate
Object
gptkbp:instanceOf
gptkb:drug
gptkbp:clinicalTrialPhase
Phase 1/2
gptkbp:developedBy
gptkb:Stoke_Therapeutics
gptkbp:intendedUse
gptkb:Dravet_syndrome
gptkbp:mechanismOfAction
gptkb:antisense_oligonucleotide
gptkbp:orphanDrugDesignation
gptkb:FDA
gptkb:EMA
gptkbp:routeOfAdministration
intrathecal
gptkbp:status
investigational
gptkbp:targetGene
gptkb:SCN1A
gptkbp:therapeuticArea
neurology
gptkbp:bfsParent
gptkb:Stoke_Therapeutics
gptkbp:bfsLayer
7
https://www.w3.org/2000/01/rdf-schema#label
STK-001