Statements (14)
Predicate | Object |
---|---|
gptkbp:instanceOf |
gptkb:drug
|
gptkbp:clinicalTrialPhase |
Phase 1/2
|
gptkbp:developedBy |
gptkb:Stoke_Therapeutics
|
https://www.w3.org/2000/01/rdf-schema#label |
STK-001
|
gptkbp:intendedUse |
gptkb:Dravet_syndrome
|
gptkbp:mechanismOfAction |
antisense oligonucleotide
|
gptkbp:orphanDrugDesignation |
gptkb:FDA
gptkb:EMA |
gptkbp:routeOfAdministration |
intrathecal
|
gptkbp:status |
investigational
|
gptkbp:targetGene |
gptkb:SCN1A
|
gptkbp:therapeuticArea |
neurology
|
gptkbp:bfsParent |
gptkb:Stoke_Therapeutics
|
gptkbp:bfsLayer |
7
|