Prevail Therapeutics

GPTKB entity

Statements (63)
Predicate Object
gptkbp:instance_of gptkb:biotechnology
gptkbp:acquired_by gptkb:Eli_Lilly_and_Company
gptkbp:advocacy engagement with communities
gptkbp:biotechnology_innovation gene editing technologies
gptkbp:biotechnology_sector innovative therapies
gptkbp:ceo Asher Cohen
gptkbp:clinical_trial patient safety
volunteers
biomarkers
multiple locations
Phase 2
safety and efficacy
efficacy studies
published data
adaptive trials
Phase 1/2
quality of life measures
NCT04023901
NCT04522612
gptkbp:collaboration AAV gene therapy
gptkbp:collaborations biopharmaceutical companies
academic partnerships
gptkbp:focus gptkb:gene_therapy
gptkbp:focuses_on gptkb:gene_therapy
gptkbp:founded gptkb:2017
gptkbp:founder Asher Cohen
gptkbp:funding gptkb:venture_capital
government grants
private funding
gptkbp:future_goals expand therapeutic pipeline.
gptkbp:goal disease modification
gptkbp:has_advisory_board experts in gene therapy
gptkbp:headquarters gptkb:New_York_City
https://www.w3.org/2000/01/rdf-schema#label Prevail Therapeutics
gptkbp:industry gptkb:pharmaceuticals
gptkbp:instruction_set multiple product candidates
gptkbp:invention gene therapy technologies
gptkbp:investment $100 million
institutional investors
gptkbp:leadership biotech industry veterans
gptkbp:location gptkb:United_States
gptkbp:mission transform lives through gene therapy.
gptkbp:notable_products PR001
PR006
gptkbp:partnership gptkb:Duke_University
gptkb:University_of_Pennsylvania
research institutions
gptkbp:patient_population neurodegenerative disease patients
gptkbp:publications peer-reviewed journals
gptkbp:regulatory_compliance FDA approved
FDA submissions
gptkbp:research clinical trials
gptkbp:research_areas neurology
gene delivery systems
gptkbp:research_focus gptkb:neurodegenerative_diseases
rare diseases
gptkbp:specializes_in gptkb:neurodegenerative_diseases
gptkbp:targets gptkb:neurodegenerative_diseases
gptkbp:technology AAV vector
gptkbp:traded_on gptkb:NASDAQ
gptkbp:type gptkb:public_company
gptkbp:type_of gptkb:public_company
gptkbp:website www.prevailtherapeutics.com