Mitochondrial Pyruvate Carrier Deficiency

GPTKB entity

Statements (22)
Predicate Object
gptkbp:instanceOf gptkb:genetic_disorder
gptkb:metabolic_disorder
gptkbp:affects mitochondrial pyruvate transport
gptkbp:cause hypotonia
failure to thrive
lactic acidosis
neurodevelopmental delay
gptkbp:diagnosedBy genetic testing
metabolic studies
gptkbp:firstDescribed 2012
gptkbp:inheritance autosomal recessive
gptkbp:mutationAssociatedWith gptkb:MPC1_gene
gptkb:MPC2_gene
gptkbp:OMIM 614741
gptkbp:symptom muscle weakness
seizures
developmental delay
elevated lactate levels
gptkbp:treatment supportive care
gptkbp:bfsParent gptkb:MPD
gptkbp:bfsLayer 6
https://www.w3.org/2000/01/rdf-schema#label Mitochondrial Pyruvate Carrier Deficiency