mucopolysaccharidosis IVA

E2210250 UNEXPLORED

Mucopolysaccharidosis IVA (Morquio A syndrome) is a rare inherited lysosomal storage disorder characterized by deficient degradation of certain glycosaminoglycans, leading to progressive skeletal abnormalities and other systemic complications.

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All labels observed (1)

Label Occurrences
mucopolysaccharidosis IVA canonical 1

Referenced by (1)

Full triples — surface form annotated when it differs from this entity's canonical label.

BioMarin Pharmaceutical developsTreatmentFor mucopolysaccharidosis IVA