Translarna

E1550454 UNEXPLORED

Translarna is a precision medicine developed by PTC Therapeutics to treat genetic disorders caused by nonsense mutations, such as certain forms of Duchenne muscular dystrophy.

All labels observed (1)

Label Occurrences
Translarna canonical 1

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Full triples — surface form annotated when it differs from this entity's canonical label.

PTC Therapeutics hasDrug Translarna